Scientists in the Netherlands have made a discovery that may advance the treatment of the genetic disorder known as Pompe disease. Along with co-workers in England, they found a possible blocker to halt the disease’s progression, which might also aid in the development of diagnostics and treatments for Gaucher disease. The study, “…
News
Recent Posts
- VPRIV shows some benefits for bone health in Gaucher disease type 1
- Long-term Cerezyme use improves health, growth for kids with Gaucher
- When you’re stuck on the hamster wheel of figuring out what’s wrong
- New mRNA therapy aims to restore missing enzyme in Gaucher: Study
- Blood cancer warning signs common in adults with Gaucher: Study