How can I turn a ripple into a giant ocean? How can my ripple have a lasting impact when there are thousands of ripples just like mine? How can I weather a storm that I’m not sure will ever end? For the longest time, I struggled to come to terms…
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The first patient has been dosed in a global clinical trial testing the safety and efficacy of FLT201 (avigbagene parvec), an investigational gene therapy that Spur Therapeutics is developing for Gaucher disease type 1. The Phase 3Â trial (NCT07223944) is recruiting up to 45 adults with Gaucher disease…
One of the questions I never expected to face as a parent is how to explain a chronic illness to a toddler. My son is almost 2 years old, which means he doesn’t understand much about Gaucher disease. He doesn’t know what a genetic disorder is, why I need…
