I recently wrote a column about how I don’t really feel “sick” with Gaucher disease. Looking back, though, I don’t think that column told the whole story. I’m currently dealing with some other medical issues, and when you already have a chronic condition, everything somehow feels connected. A…
The first patient has been dosed in a global clinical trial testing the safety and efficacy of FLT201 (avigbagene parvec), an investigational gene therapy that Spur Therapeutics is developing for Gaucher disease type 1. The Phase 3Â trial (NCT07223944) is recruiting up to 45 adults with Gaucher disease…
How can I turn a ripple into a giant ocean? How can my ripple have a lasting impact when there are thousands of ripples just like mine? How can I weather a storm that I’m not sure will ever end? For the longest time, I struggled to come to terms…
