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About Gaucher disease
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What is Gaucher disease?
Types
Causes
Symptoms
Diagnosis
Treatments
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Approved treatments
Enzyme replacement therapy
Cerezyme
Elelyso
VPRIV
Substrate reduction therapy
Cerdelga
Zavesca
Experimental treatments
Chaperone therapy
Ambroxol hydrochloride
Gene therapy
FLT201
PR001
Non-drug treatments
Orthopedic surgery
Pain management
Physiotherapy
Splenectomy
Stem cell transplant
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The Gaucher Guide to Grace —
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Poshala Aluwihare, —
Articles by Poshala Aluwihare
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