Dantrolene could be a new therapeutic agent to improve neurological function and disease symptoms in neuropathic Gaucher disease (nGD), according…
Articles by Malika Ammam, PhD
Researchers investigating the long-term efficacy and safety of taliglucerase alfa in treatment-naïve adults with Gaucher disease (GD) reported that the drug provided…
Dr. Roscoe Owen Brady, a long honored pioneer for enzyme therapeutic approaches in treating metabolic disorders including Gaucher disease, has…
A team of researchers led by the University of Victoria, British Columbia, have recently identified two novel mutation sites…
The biochemical responses in patients with Gaucher disease type I (GD1) treated with some selected therapeutic options have been compared…
The diagnostic and therapeutic approaches in children living in Iraq with Gaucher disease (GD) were recently evaluated in a study, “…
A team of researchers recently discussed the recommended uses of the drug eliglustat in American adults suffering from Gaucher disease…