• Latest NORD Webinar Offers Insights on Starting Nonprofit, Patient Registry
  • UK Mom Knows Fight Far From Over After Losing Baby to Gaucher Type 2
  • NORD Hosting ‘RareLaunch’ Workshops to Help Start Rare Disease Non-profits
  • Potential Gene Therapy for Type 2 Gaucher, PR001, Placed on FDA Fast Track
  • UK Organization ‘Same But Different’ Announces ‘Glimmer of Hope’ Photo Contest Winner
  • Neuronopathic Gaucher Immune Response Might Protect Brain From Infection
  • Telehealth ‘Helpful’ Alternative to In-person Care, Rare Disease Patients Say
  • Online Awareness Campaigns Aim to Magnetize Supporters Worldwide
  • Gaucher Type 1 Therapy AVR-RD-02 Granted EU Orphan Drug Status
  • Same But Different Asks Public to Vote on ‘Glimmer of Hope’ Calendar Photos
  • Efforts Continue Beyond Awareness Month to Expand Newborn Screening Panels in US
  • Potential SRT for Neuronopathic Gaucher Shows Efficacy in Early Study