• Cerdelga Continuously Provides Long-term Benefits for Gaucher Patients, Study Shows
  • Advocacy Groups, Doctors Question Rising Prices of Rare Disease Treatments
  • Worsening of Untreated Retinal Detachment in Boy with Gaucher Type 3 Described in Case Report
  • AVROBIO Advances AVR-RD-02 Gene Therapy into Gaucher Disease Phase 1/2 Trial in Canada
  • Lab-grown Bone Cells May Predict Gaucher Patients’ Response to Bone Disease Therapy
  • #NORDSummit – More Than 700 Expected to Attend Oct. 15-16 Rare Disease Summit in Washington
  • Oral Medication Linked to Better Quality of Life Over Infusion Therapy in Gaucher Disease, Study Suggests
  • Liver Fibrosis Common in Gaucher Type 1, and ERT Is Seen to Be Beneficial, Study Reports
  • Early Gene Therapy Holds Promise to Treat Gaucher Disease, Mouse Study Shows
  • Sanofi’s Cerezyme Should Be Administered Under Current Guidelines with Potential for Change, Study Says
  • Multiparametric MRI May Help Identify, Monitor Bone Lesions in Gaucher Patients, Study Suggests
  • Type 3 Gaucher Disease Is Most Common Subtype in Filipinos, Study Shows